Game changer for #sicklecellamemia.
doi.org/10.1182/blooda…
Nonmyleoablative haploBMT with PTCy using Baltimore regimen (flu/cy/tbi400) rather than thiotepa.
What are the advances? 1) 95% OS and 94% DFS @ 2.4 yrs 2)ONLY curative therapy that preserves FERTILITY!
doi.org/10.1182/blooda…
Nonmyleoablative haploBMT with PTCy using Baltimore regimen (flu/cy/tbi400) rather than thiotepa.
What are the advances? 1) 95% OS and 94% DFS @ 2.4 yrs 2)ONLY curative therapy that preserves FERTILITY!