We are finally here. Thanks to @OscarWilkins16 and @FrattaLab gave me this wonderful chance to participate in this fantastic research.
Creation of de novo cryptic splicing for ALS and FTD precision medicine | Science science.org/doi/10.1126/sc…
Creation of de novo cryptic splicing for ALS and FTD precision medicine | Science science.org/doi/10.1126/sc…
www.science.org Creation of de novo cryptic splicing for ALS and FTD precision medicine Loss of function of the RNA-binding protein TDP-43 (TDP-LOF) is a hallmark of amyotrophic lateral sclerosis (ALS) and other neurodegenerative disorders. Here we describe TDP-REG, which exploits the... 
