Parent Project Muscular Dystrophy (PPMD)

What better moment to introduce the #SurgetoSaveNewborns Act than #NewbornScreeningAwarenessMonth? Now is the time to urge Congress to pass this critical legislation: surgetosave.org/act-now/

September 7th is World Duchenne Awareness Day! On this day, the global Duchenne community comes together to raise our voices for #Duchenne and #Becker. This year we recognize the importance of access for our community. Share your story this September 7th on #WDAD2026.

Today, @Capricor announced that the FDA has accepted the company’s amendment to the BLA for Deramiocel, and the FDA will be extending the current PDUFA action date to November 22, 2026.

Learn more and catch up on recent Deramiocel updates: parentprojectmd.org/update-on-dera…

As we approach FDA’s current 8/22 PDUFA date for Deramiocel, the #Duchenne community is watching closely for an update. We've requested an update from @Capricor and will share information with the community as soon as possible. parentprojectmd.org/deramiocel-whe…

The next PPMD Livestream with the PAAC is coming Thursday 8/27 at 4 PM ET! Join us for real-life tech tips, tools, and hacks to make life more accessible, manageable, and independent for people living with #Duchenne or #Becker. Tune in next week! facebook.com/share/1L3qzFff…