This is my last-ever post on X. Since Twitter changed to X, the platform has become toxic and full of misinformation and disinformation. In the future I will be posting on LinkedIn and BlueSky.
Michael Makris
@ProfMakris
Emeritus Professor of Haemostasis and Thrombosis in Sheffield, UK. I tweet about thrombosis, hemophilia, COVID-19, medicine, NHS & AI. Opinions are my own.
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Latest posts 5
Today is #WorldHemophiliaDay and this year's theme is that women and girls bleed too. Despite the development of brilliant treatments to treat severe #hemophilia in primarily men, the diagnosis and treatment of women have not received as much attention.
This is the press release about the new #hemophilia B gene therapy that has been approved in China. So there are now 3 approved gene therapies for hemophilia B, 2 in US/Europe approved by the FDA/EMA and 1 in China approved by the Chinese regulator. tinyurl.com/2jc74nb9
www.prnewswire.com Belief BioMed and Takeda China jointly announced BBM-H901 (Dalnacogene Ponparvovec Injection),... /PRNewswire/ -- Belief BioMed ("BBM") and Takeda China today jointly announced that BBM-H901 (generic name: Dalnacogene Ponparvovec Injection), has been... Thank you for the copies of the paper on the UK Infected Blood Inquiry that was published in @BloodJournal. It is interesting to see the section on lessons learned. Despite the @bloodinquiry, the UK continues to use cryo and FFP without viral inactivation. #hemophilia
Any idea of the price of this, @Brianhemophilia? Presumably there is nothing to stop patients from traveling to China to have it. It is difficult to believe it will cost anything remotely close to Hemgenix.
Belief Biomed and Takeda China announce licencing by the National Medical Products Administration ( NMPA)in China of their BBM-H901 FIX Gene Therapy. Interested to see if they pursue licencing from FDA or EMA which could make it a more viable option in US or EuropeView quoted post on X
